AAV-based gene therapy prevents and halts the progression of dilated cardiomyopathy in a mouse model of phosphoglucomutase 1 deficiency (PGM1-CDG)

  • Bijina Balakrishnan
  • , Ruqaiah Altassan
  • , Rohit Budhraja
  • , Willisa Liou
  • , Arielle Lupo
  • , Sarah Bryant
  • , Anastasiya Mankouski
  • , Silvia Radenkovic
  • , Graeme J. Preston
  • , Akhilesh Pandey
  • , Sihem Boudina
  • , Tamas Kozicz
  • , Eva Morava-Kozicz
  • , Kent Lai*
    • *Corresponding author for this work

Research output: Contribution to journal › Article › peer-review

17 Citations (Scopus)

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Biochemistry, Genetics and Molecular Biology

Immunology and Microbiology